Muscular dystrophy patients get first gene therapy
In an eagerly anticipated decision, the Food and Drug Administration Thursday approved the first gen...
Duchenne muscular dystrophy
FDA advisers narrowly back first gene therapy for muscular dystrophy
In a split vote, advisers to the Food and Drug Administration recommended that the agency approve th...
Gene therapy for muscular dystrophy stirs hopes and controversy
When Chase Finazzo was just a few years old, his parents noticed Chase was pretty clumsy. But they d...